scarlet_sage t1_jcsqgqw wrote on March 19, 2023 at 7:27 AM

Reply to comment by crankyape1534 in Road to Hana, Maui, Hawaii [OC] [4010x8021] by JKeith26

Planning to go in April. What negative experiences?

scarlet_sage t1_ixvnm9y wrote on November 26, 2022 at 7:02 PM

Reply to comment by Sariel007 in A novel medication for hemophilia B has just been approved by the Food and Drug Administration. The treatment is a form of gene therapy, intended to replace a dysfunctional gene that leaves people unable to control their bleeding. by Sariel007

It did not appear to be a cure, though it doesn't explain why.

>It also appeared to lower the rate of bleeding problems by 54% in one trial, and it reduced the need for regular infusions of clotting factors....

>it should reduce the frequency of expensive transfusions; they also say that the drug’s effectiveness is expected to last for several years at least.